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Long-term Success of Cerezyme Therapy Described in New Publication


Genzyme General, a division of Genzyme Corp., today announced the publication of the most extensive set of data ever reported on the long-term effectiveness of enzyme replacement therapy with Cerezyme® (imiglucerase for injection) for patients with Type 1 Gaucher disease.

 The report, which appears in the American Journal of Medicine, describes the clinical success achieved by more than 1,000 patients worldwide followed in the Gaucher Registry who have received Cerezyme therapy for as long as five years. Data from the report were presented last week at the annual symposium of the Society for the Study of Inborn Errors of Metabolism in Dublin, Ireland.

The long-term findings described in the report build upon the results of earlier studies by showing that Cerezyme therapy reverses and prevents the progression of the major clinical manifestations of Gaucher disease. The authors concluded that patients achieved and maintained a complete or partial elimination of anemia and platelet deficiency and a reduction of the enlargement of the liver and spleen. Improvement or prevention of bone pain and bone crises was also observed. These clinical results, together with more than 11 years of safe and effective clinical use, have made Cerezyme therapy the standard of care for the treatment of individuals with Type 1 Gaucher disease.

 “The data presented result from an unprecedented collaboration between the Gaucher medical and patient communities worldwide, aimed at better understanding the impact Cerezyme therapy has had on altering the natural history of this rare hereditary disease,” said lead author Neal J. Weinreb, MD, University Hospital and Medical Center, Tamarac, Florida. “We anticipate that these results will provide a benchmark for the expectations and goals of therapy, and will help guide physicians in developing appropriate care plans for their patients with Gaucher disease.”

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למצגת הסבר על מחלת הגושה , איבחון וטיפול

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